β-thalassemias

dc.contributor.authorTaher, Ali T.
dc.contributor.authorMusallam, Khaled M.
dc.contributor.authorCappellini, Maria Teresa
dc.contributor.departmentInternal Medicine
dc.contributor.facultyFaculty of Medicine (FM)
dc.contributor.institutionAmerican University of Beirut
dc.date.accessioned2025-01-24T11:43:28Z
dc.date.available2025-01-24T11:43:28Z
dc.date.issued2021
dc.identifier.doihttps://doi.org/10.1056/NEJMra2021838
dc.identifier.eid2-s2.0-85101657020
dc.identifier.pmid33626255
dc.identifier.urihttp://hdl.handle.net/10938/30292
dc.language.isoen
dc.publisherMassachussetts Medical Society
dc.relation.ispartofNew England Journal of Medicine
dc.sourceScopus
dc.subjectActivin receptors, type ii
dc.subjectBeta-thalassemia
dc.subjectErythrocyte transfusion
dc.subjectGenetic therapy
dc.subjectGenotype
dc.subjectHematinics
dc.subjectHematopoietic stem cell transplantation
dc.subjectHumans
dc.subjectImmunoglobulin fc fragments
dc.subjectIron overload
dc.subjectPhenotype
dc.subjectRecombinant fusion proteins
dc.subjectCreatinine
dc.subjectDeferasirox
dc.subjectDeferiprone
dc.subjectDeferoxamine
dc.subjectHemoglobin
dc.subjectLiver enzyme
dc.subjectLuspatercept
dc.subjectPlacebo
dc.subjectActivin receptor 2
dc.subjectAntianemic agent
dc.subjectFusion protein
dc.subjectImmunoglobulin fc fragment
dc.subjectAgranulocytosis
dc.subjectArthralgia
dc.subjectBeta thalassemia
dc.subjectBlood transfusion
dc.subjectBone disease
dc.subjectBone pain
dc.subjectClinical feature
dc.subjectDizziness
dc.subjectDna determination
dc.subjectDrug hypersensitivity
dc.subjectEar disease
dc.subjectEye disease
dc.subjectFamily history
dc.subjectGastrointestinal symptom
dc.subjectGene therapy
dc.subjectGenotype phenotype correlation
dc.subjectGeographic distribution
dc.subjectHemoglobin synthesis
dc.subjectHuman
dc.subjectHypertension
dc.subjectHyperuricemia
dc.subjectIron chelation
dc.subjectMedical history
dc.subjectMolecular pathology
dc.subjectNeutropenia
dc.subjectNonhuman
dc.subjectPatient care
dc.subjectPhysical examination
dc.subjectPsychosocial care
dc.subjectReview
dc.subjectSide effect
dc.subjectThrombosis
dc.subjectAdverse event
dc.subjectComplication
dc.subjectGenetics
dc.titleβ-thalassemias
dc.typeReview

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