β-thalassemias
| dc.contributor.author | Taher, Ali T. | |
| dc.contributor.author | Musallam, Khaled M. | |
| dc.contributor.author | Cappellini, Maria Teresa | |
| dc.contributor.department | Internal Medicine | |
| dc.contributor.faculty | Faculty of Medicine (FM) | |
| dc.contributor.institution | American University of Beirut | |
| dc.date.accessioned | 2025-01-24T11:43:28Z | |
| dc.date.available | 2025-01-24T11:43:28Z | |
| dc.date.issued | 2021 | |
| dc.identifier.doi | https://doi.org/10.1056/NEJMra2021838 | |
| dc.identifier.eid | 2-s2.0-85101657020 | |
| dc.identifier.pmid | 33626255 | |
| dc.identifier.uri | http://hdl.handle.net/10938/30292 | |
| dc.language.iso | en | |
| dc.publisher | Massachussetts Medical Society | |
| dc.relation.ispartof | New England Journal of Medicine | |
| dc.source | Scopus | |
| dc.subject | Activin receptors, type ii | |
| dc.subject | Beta-thalassemia | |
| dc.subject | Erythrocyte transfusion | |
| dc.subject | Genetic therapy | |
| dc.subject | Genotype | |
| dc.subject | Hematinics | |
| dc.subject | Hematopoietic stem cell transplantation | |
| dc.subject | Humans | |
| dc.subject | Immunoglobulin fc fragments | |
| dc.subject | Iron overload | |
| dc.subject | Phenotype | |
| dc.subject | Recombinant fusion proteins | |
| dc.subject | Creatinine | |
| dc.subject | Deferasirox | |
| dc.subject | Deferiprone | |
| dc.subject | Deferoxamine | |
| dc.subject | Hemoglobin | |
| dc.subject | Liver enzyme | |
| dc.subject | Luspatercept | |
| dc.subject | Placebo | |
| dc.subject | Activin receptor 2 | |
| dc.subject | Antianemic agent | |
| dc.subject | Fusion protein | |
| dc.subject | Immunoglobulin fc fragment | |
| dc.subject | Agranulocytosis | |
| dc.subject | Arthralgia | |
| dc.subject | Beta thalassemia | |
| dc.subject | Blood transfusion | |
| dc.subject | Bone disease | |
| dc.subject | Bone pain | |
| dc.subject | Clinical feature | |
| dc.subject | Dizziness | |
| dc.subject | Dna determination | |
| dc.subject | Drug hypersensitivity | |
| dc.subject | Ear disease | |
| dc.subject | Eye disease | |
| dc.subject | Family history | |
| dc.subject | Gastrointestinal symptom | |
| dc.subject | Gene therapy | |
| dc.subject | Genotype phenotype correlation | |
| dc.subject | Geographic distribution | |
| dc.subject | Hemoglobin synthesis | |
| dc.subject | Human | |
| dc.subject | Hypertension | |
| dc.subject | Hyperuricemia | |
| dc.subject | Iron chelation | |
| dc.subject | Medical history | |
| dc.subject | Molecular pathology | |
| dc.subject | Neutropenia | |
| dc.subject | Nonhuman | |
| dc.subject | Patient care | |
| dc.subject | Physical examination | |
| dc.subject | Psychosocial care | |
| dc.subject | Review | |
| dc.subject | Side effect | |
| dc.subject | Thrombosis | |
| dc.subject | Adverse event | |
| dc.subject | Complication | |
| dc.subject | Genetics | |
| dc.title | β-thalassemias | |
| dc.type | Review |
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